Background:
Lenvatinib is a multikinase inhibitor of VEGFR 1−3, FGFR 1−4, PDGFRα, RET, and KIT. Pembrolizumab, an antibody targeting PD-1, prevents T cell deactivation. In addition to its antiangiogenic effects, lenvatinib may act, in part, by preventing VEGF-mediated immune suppression, suggesting combination with pembrolizumab could improve its activity. From a phase 1b/2 trial of lenvatinib+pembrolizumab, we report results in pts with endometrial carcinoma.
Methods:
In this multicenter, open-label study, pts had confirmed metastatic endometrial cancer that progressed after approved therapy, measurable disease, and ECOG PS ≤1. Pts received oral lenvatinib 20 mg/day + pembrolizumab 200 mg intravenously every 3 weeks, with tumor assessments by the investigator. The primary phase 2 endpoint was ORR based on irRECIST. Secondary endpoints included PFS, DCR (complete response [CR]+ partial response [PR]+ stable disease [SD]), CBR (CR + PR + durable SD), and duration of response (DOR), all by irRECIST, and safety.
Results:
Twenty-three patients enrolled (phase 2: 21; phase 1b: 2); median age was 64 years (range: 51−80); 87% were white; and all had ≥1 prior anticancer therapy. Confirmed ORR was 48% (all PR). Median PFS and DOR were not estimable (NE; see table). All pts had treatment-emergent adverse events, with hypertension, fatigue, arthralgia, diarrhea, and nausea as the most common. Toxicities were manageable with dose interruption and/or modification and no new safety signals occurred. Updated data will be presented.
Conclusions:
Promising efficacy was observed in pts receiving lenvatinib+pembrolizumab, and toxicities were generally expected and manageable with dose modification. These results warrant further study of lenvatinib+pembrolizumab in patients with endometrial carcinoma.
Parameter |
Patients (n=23) |
95% CI |
ORR, n (%) |
11 (48%) |
27−69 |
DCR, n (%) |
22 (96%) |
78−100 |
CBR, n (%) |
17 (74%) |
52−90 |
Median PFS, months |
NE |
4.1−NE |
Median DOR, months* |
NE |
2.6−NE |
*For patients with CR or PR
CI, confidence interval.